IDH1 Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
46Targets
958Trials
16Drugs
0Datasets
4,188Sources
10,439Claims
10,589Evidence
1,574Hypotheses
DRUGapproved

Enasidenib

Mechanism

FDA-approved for IDH2-mutant AML. Potential for IDH2-escape in CCA.

Related claims (50)

TypePredicateConfSource
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug targetEnasidenib (AG-221) is a selective inhibitor targeting mutant IDH2.100%40965018
drug efficacyInhibitors of mutated IDH1 and IDH2, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug targetInhibitors of mutated IDH1 and IDH2 are vorasidenib, ivosidenib, olutasidenib, and enasidenib.100%41662580
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug efficacyInhibitors of mutated IDH1 and IDH2, enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug efficacyInhibitors of mutated IDH1 and IDH2, enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetEnasidenib is an oral IDH2 inhibitor that reduces the production of the oncometabolite 2-hydroxyglutarate (clinical trial result).95%40650712
safetyEnasidenib treatment in IDH2-mutated myeloid neoplasms was associated with drug-related leukocytosis in 21.7% of patients, hyperbilirubinemia in 26.1%, and differentiation syndrome in 17.4% (observed in patient cohort).94%40650712
survivalPatients with IDH2-mutated AML who achieved complete response with enasidenib had significantly better median overall survival (19.8 months vs. 4.2 months, p = 0.01) compared to those who did not achieve complete response (observed in patie...93%40650712
drug efficacyIn a Spanish multicenter real-life study, enasidenib achieved an overall response rate (ORR) of 39.1% and a morphological complete remission (CR) rate of 26.1% in IDH2-mutated myeloid neoplasms (observed in patient cohort).92%40650712
drug efficacyThe IDH inhibitors enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug efficacyThe IDH inhibitors enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug targetEnasidenib is an inhibitor of mutated IDH2.90%41662580
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug targetIDH1/2 inhibitors (ivosidenib, olutasidenib, and enasidenib) are currently used to treat leukemias.90%41761287
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyVorasidenib, ivosidenib, olutasidenib, and enasidenib were recently approved by the FDA for relapsed/refractory AML.90%41662580
drug targetIDH1/2 inhibitors (ivosidenib, olutasidenib, and enasidenib) are currently used to treat leukemias.90%41761287
drug targetIDH1/2 inhibitors (ivosidenib, olutasidenib, and enasidenib) are currently used to treat leukemias.90%41761287
drug targetVorasidenib, ivosidenib, olutasidenib, and enasidenib are inhibitors of mutated IDH1 and IDH2, respectively.90%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML.90%41662580
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug efficacyThe IDH inhibitors ivosidenib and enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug efficacyIDH1/2 inhibitors (ivosidenib, enasidenib, olutasidenib) yield overall response rates (ORRs) of 30-94% in AML with DS (clinical trial result).90%41751911
drug targetIDH1/2 inhibitors (ivosidenib, olutasidenib, and enasidenib) are currently used to treat leukemias.90%41761287
drug efficacyThe IDH inhibitors enasidenib have shown significant clinical benefits in patients with IDH mutations (clinical trial result).90%39721469

Off-Target Findings (4)

untiered: 4
TargetRoleTierBoltz-2 iPTMChai-1 iPTMVerdict
KDM6ASMA0.865
IDH1_WTOTHER0.754
IDH1_R132HOTHER0.674
TET2_catalyticOTHER0.480