IDH1 Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
46Targets
958Trials
16Drugs
0Datasets
4,188Sources
10,439Claims
10,589Evidence
1,574Hypotheses
DRUGapproved

Ivosidenib

Mechanism

FDA/EMA-approved for IDH1-mutant CCA. Oral, 500mg daily. ClarIDHy trial: mPFS 2.7 vs 1.4mo.

Related claims (50)

TypePredicateConfSource
drug efficacyIvosidenib is used to treat cholangiocarcinoma.100%39926494
drug efficacyIvosidenib (AG-120) is approved by the FDA for the treatment of IDH1-mutated cholangiocarcinoma (clinical trial result).100%40183465
drug efficacyIvosidenib is approved for advanced intrahepatic cholangiocarcinoma (ICC) with mutant IDH1 (mIDH1).100%41460204
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyIvosidenib is approved in the EU and USA for the treatment of adults with pretreated, advanced, mIDH1 cholangiocarcinoma (CCA).100%37855990
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetIvosidenib is an FDA-approved inhibitor for IDH1.100%41102000
drug efficacyKnockdown of ALYREF or treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo (observed in mouse model).100%40369958
drug targetIvosidenib is a potent and selective inhibitor of mutant isocitrate dehydrogenase 1 (mIDH1).100%37855990
drug efficacyTreatment with ivosidenib (an IDH1 inhibitor) (observed in mouse model) significantly suppressed tumor growth in vivo.100%40369958
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug targetIvosidenib (IVO) is used for the treatment of cholangiocarcinoma.100%38617799
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyTreatment with ivosidenib (an IDH1 inhibitor) (observed in mouse model) significantly suppressed tumor growth in vivo.100%40369958
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug targetIvosidenib is approved for pre-treated advanced CCA targeting IDH1 mutations.100%37760415
drug targetIvosidenib is an IDH1 inhibitor (clinical trial result).100%41868199
drug targetIvosidenib is an FDA-approved inhibitor for IDH1.100%41102000
drug efficacyIn a xenograft tumor mouse model, treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo.100%40369958
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug efficacyIvosidenib is an FDA-approved targeted therapy for patients with cholangiocarcinoma (clinical trial result).100%41226789
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug efficacyIvosidenib is used to treat cholangiocarcinoma.100%39926494
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug efficacyIvosidenib is used to treat cholangiocarcinoma.100%39926494
drug targetIvosidenib is an IDH1 inhibitor.100%40369958
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug efficacyIvosidenib is an FDA-approved targeted therapy for patients with cholangiocarcinoma (clinical trial result).100%41226789
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug targetEnasidenib and ivosidenib are targeted therapies for AML that target IDH1/2.100%41893037
drug efficacyKnockdown of ALYREF or treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo (observed in mouse model).100%40369958
drug efficacy(observed in mouse model) Treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo.100%40369958
drug efficacyIvosidenib has been approved in Korea for BTC patients with IDH1 mutations.100%40033637
drug efficacy(observed in mouse model) Treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo.100%40369958
drug efficacy(observed in mouse model) Treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo.100%40369958
drug targetIvosidenib is used to treat cholangiocarcinoma.100%39926494
drug efficacyIvosidenib is used to treat cholangiocarcinoma.100%39926494
drug efficacyIn the ClarIDHy study in patients with pretreated, advanced mIDH1 CCA, monotherapy with ivosidenib almost doubled the disease control rate compared with placebo (clinical trial result).100%37855990
drug efficacyKnockdown of ALYREF or treatment with ivosidenib (an IDH1 inhibitor) significantly suppressed tumor growth in vivo (observed in mouse model).100%40369958
drug efficacyIvosidenib is indicated for the treatment of locally advanced or metastatic cholangiocarcinoma.100%39097182
drug targetIvosidenib (IVO) is used for the treatment of cholangiocarcinoma.100%38617799
drug efficacyIvosidenib is used to treat cholangiocarcinoma.100%39926494

Off-Target Findings (5)

untiered: 5
TargetRoleTierBoltz-2 iPTMChai-1 iPTMVerdict
IDH1_WTOTHER0.833
KDM6ASMA0.773
TET2_catalyticOTHER0.754
IDH1_R132HOTHER0.742
IDH2_R140QOTHER0.576