IDH1 Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
46Targets
958Trials
16Drugs
0Datasets
4,188Sources
10,439Claims
10,589Evidence
1,574Hypotheses
DRUGapproved

Pemigatinib

Mechanism

For FGFR2 fusion/rearrangement iCCA only.

Related claims (50)

TypePredicateConfSource
drug efficacy(clinical trial result) Pemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions in September 2021.100%40710216
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug efficacyPemigatinib has been approved in Korea for BTC patients with FGFR2 fusions.100%40033637
drug efficacy(clinical trial result) Nearly half of patients with pretreated, advanced CCA harbouring an FGFR2 fusion or rearrangement who received pemigatinib had stable disease.100%38206555
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
survival(clinical trial result) Median progression-free survival in patients with pretreated, advanced CCA harbouring an FGFR2 fusion or rearrangement who received pemigatinib was 7.0 months.100%38206555
drug efficacy(clinical trial result) Just over a third of patients with pretreated, advanced CCA harbouring an FGFR2 fusion or rearrangement who received pemigatinib had an objective response.100%38206555
drug efficacyPemigatinib has been approved in Korea for BTC patients with FGFR2 fusions.100%40033637
drug efficacyPemigatinib is an FDA-approved targeted therapy for patients with cholangiocarcinoma (clinical trial result).100%41226789
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug efficacyVPS33A knockdown increased cellular sensitivity to Pemigatinib (demonstrated in vitro).100%41718964
drug efficacy(observed in patient cohort) The physician-assessed disease control rate was 89% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacy(observed in patient cohort) The physician-assessed objective response rate was 56% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacyPemigatinib is approved for patients with cholangiocarcinoma harboring FGFR2 fusions and/or rearrangements (clinical trial result).100%38424198
drug efficacyInfigratinib and Pemigatinib are approved for use in cholangiocarcinoma patients with FGFR2 fusions (clinical trial result).100%38653586
drug efficacy(observed in patient cohort) The physician-assessed disease control rate was 89% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacy(observed in patient cohort) A PFS comparable to that in the phase 2 FIGHT-202 trial was reported with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacyInfigratinib and Pemigatinib are approved for use in cholangiocarcinoma patients with FGFR2 fusions (clinical trial result).100%38653586
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacy(observed in patient cohort) The physician-assessed objective response rate was 56% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacyPemigatinib is an approved targeted therapy for CCA (clinical trial result)100%41226789
drug efficacy(observed in patient cohort) A PFS comparable to that in the phase 2 FIGHT-202 trial was reported with pemigatinib use in this Canadian PSP cohort.100%40710216
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug efficacy(observed in patient cohort) The physician-assessed disease control rate was 89% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug efficacyInfigratinib and Pemigatinib are approved for use in cholangiocarcinoma patients with FGFR2 fusions (clinical trial result).100%38653586
drug efficacy(observed in patient cohort) The physician-assessed disease control rate was 89% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacy(clinical trial result) Pemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions in September 2021.100%40710216
drug targetPemigatinib is an inhibitor of fibroblast growth factor receptor (FGFR) 1-3.100%38206555
drug efficacy(observed in patient cohort) A PFS comparable to that in the phase 2 FIGHT-202 trial was reported with pemigatinib use in this Canadian PSP cohort.100%40710216
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug efficacy(observed in patient cohort) The physician-assessed objective response rate was 56% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacy(clinical trial result) Pemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions in September 2021.100%40710216
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacy(clinical trial result) Pemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions in September 2021.100%40710216
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug targetPemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions.100%40710216
drug efficacy(observed in patient cohort) The physician-assessed objective response rate was 56% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacy(observed in patient cohort) The physician-assessed objective response rate was 56% with pemigatinib use in this Canadian PSP cohort.100%40710216
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacy(clinical trial result) Pemigatinib received Health Canada approval for previously treated locally advanced/metastatic cholangiocarcinoma (CCA) with <i>FGFR2</i> rearrangements/fusions in September 2021.100%40710216
drug efficacyPemigatinib has been approved in Korea for BTC patients with FGFR2 fusions.100%40033637
drug efficacy(observed in patient cohort) The physician-assessed disease control rate was 89% with pemigatinib use in this Canadian PSP cohort.100%40710216
gene expressionPemigatinib-resistant RBE-R and HuCCT1-R cell lines exhibited elevated VPS33A expression (demonstrated in vitro).100%41718964
drug efficacyPemigatinib is approved for treating cholangiocarcinoma with FGFR2 fusion/rearrangement (clinical trial result).100%39583123
drug efficacyPemigatinib-resistant RBE-R and HuCCT1-R cell lines exhibited autophagy-dependent drug resistance (demonstrated in vitro).100%41718964

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.