IDH1 Research Platform

Evidence graph for Spinal Muscular Atrophy

Biology-first target discovery
Christian Fischer / Bryzant Labs
46Targets
958Trials
16Drugs
0Datasets
4,188Sources
10,439Claims
10,589Evidence
1,574Hypotheses
DRUGphase3

Vorasidenib

Mechanism

Dual IDH1/2 inhibitor. Approved for glioma, investigating in CCA.

Related claims (50)

TypePredicateConfSource
drug targetVorasidenib is an inhibitor of mutant IDH1/2 enzymes.100%41201564
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetInhibitors of mutated IDH1 and IDH2 are vorasidenib, ivosidenib, olutasidenib, and enasidenib.100%41662580
drug targetVorasidenib (AG-881) is a dual inhibitor which acts on both IDH1 and IDH2 mutations.100%40965018
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML (clinical trial result).100%41662580
drug targetVorasidenib is an inhibitor of mutant IDH1/2 enzymes.100%41201564
drug efficacyVorasidenib is approved for patients with mutant IDH low-grade glioma.100%41201564
drug efficacyVorasidenib is approved for patients with mutant IDH low-grade glioma.90%41201564
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib, ivosidenib, olutasidenib, and enasidenib were recently approved by the FDA for relapsed/refractory AML.90%41662580
drug efficacyInhibiting IDH mutations with vorasidenib lowers D-2HG (clinical trial result).90%41252576
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyVorasidenib, an IDH inhibitor, demonstrates promising activity in IDH-mutant low-grade gliomas (clinical trial result).90%40315665
drug targetVorasidenib, ivosidenib, olutasidenib, and enasidenib are inhibitors of mutated IDH1 and IDH2, respectively.90%41662580
drug efficacyInhibitors of mutated IDH1 and IDH2, vorasidenib, ivosidenib, olutasidenib, and enasidenib, respectively, were recently approved by the FDA for relapsed/refractory AML.90%41662580
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug targetPHGDH drives intrinsic resistance to vorasidenib by converting α-KG to D-2HG and maintaining D-2HG concentration despite IDHm inhibition (observed in patient-derived models and patient tissue)90%40950009
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyInhibiting IDH mutations with vorasidenib is beneficial to patients (clinical trial result).90%41252576
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyInhibiting IDH mutations with vorasidenib lowers D-2HG (clinical trial result).90%41252576
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib suppresses D-2HG production and extends progression-free survival in some IDHm glioma patients (clinical trial result)90%40950009
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyInhibiting IDH mutations with vorasidenib is beneficial to patients (clinical trial result).90%41252576
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyThe phase III INDIGO trial has demonstrated superiority of vorasidenib, a brain-penetrant pan-mutant IDH inhibitor, over placebo in people with non-enhancing grade 2 IDH-mutant gliomas following surgery (clinical trial result).90%38760442
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacyVorasidenib has received FDA approval for IDH-mutant gliomas (clinical trial result).90%40675687
drug efficacySelective inhibitors of mutant IDH, such as ivosidenib and vorasidenib, have been shown to reduce D-2-HG levels (demonstrated in preclinical models).80%38760442
drug efficacySelective inhibitors of mutant IDH, such as ivosidenib and vorasidenib, have been shown to reduce D-2-HG levels (demonstrated in preclinical models).80%38760442
biomarkerDeuterium metabolic imaging of D-2HG production from diethyl-[3,3'- 2 H]-α-ketoglutarate provides an early readout of response and resistance to vorasidenib (observed in patient-derived models and patient tissue)80%40950009
drug efficacySelective inhibitors of mutant IDH, such as ivosidenib and vorasidenib, have been shown to induce cellular differentiation (demonstrated in preclinical models).80%38760442
drug efficacySelective inhibitors of mutant IDH, such as ivosidenib and vorasidenib, have been shown to reduce D-2-HG levels (demonstrated in preclinical models).80%38760442
drug efficacySelective inhibitors of mutant IDH, such as ivosidenib and vorasidenib, have been shown to induce cellular differentiation (demonstrated in preclinical models).80%38760442

Off-Target Findings (0)

No Boltz-2 / Chai-1 off-target panel claims recorded for this drug.